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2. FDA considers first CRISPR gene editing treatment that may ...

   www.aol.com/fda-considers-first-crispr-gene...

   With sickle cell disease — also called sickle cell anemia — red blood cells take on a folded or sickle shape that can clog tiny blood vessels and cause progressive organ damage and pain, and ...

3. Exagamglogene autotemcel - Wikipedia

   en.wikipedia.org/wiki/Exagamglogene_autotemcel

   DrugBank. DB15572. UNII. S53L777GM8. KEGG. D12749. Exagamglogene autotemcel, sold under the brand name Casgevy, is a gene therapy used for the treatment of sickle cell disease [1][3] and transfusion-dependent beta thalassemia. [1] It was developed by Vertex Pharmaceuticals and CRISPR Therapeutics.

4. FDA approves cure for sickle cell disease, the first ... - AOL

   www.aol.com/news/fda-approves-cure-sickle-cell...

   The FDA on Friday also approved a second treatment for sickle cell disease, called Lyfgenia, a gene therapy from drugmaker Bluebird Bio. Both treatments work by genetically modifying a patient’s ...

5. CRISPR gene editing - Wikipedia

   en.wikipedia.org/wiki/CRISPR_gene_editing

   CRISPR gene editing. CRISPR-Cas9. CRISPR gene editing (CRISPR, pronounced / ˈkrɪspər / "crisper", refers to " c lustered r egularly i nterspaced s hort p alindromic r epeats") is a genetic engineering technique in molecular biology by which the genomes of living organisms may be modified. It is based on a simplified version of the bacterial ...

6. Sickle cell disease - Wikipedia

   en.wikipedia.org/wiki/Sickle_cell_disease

   Sickle cell disease (SCD), also simply called sickle cell, is a group of hemoglobin-related blood disorders typically inherited. [2] The most common type is known as sickle cell anemia. [2] It results in an abnormality in the oxygen-carrying protein haemoglobin found in red blood cells. [2] This leads to a rigid, sickle -like shape under ...

7. US FDA approves two gene therapies for sickle cell disease - AOL

   www.aol.com/news/us-approves-two-gene-therapies...

   By Leroy Leo and Bhanvi Satija (Reuters) -The U.S. Food and Drug Administration (FDA) on Friday approved two gene therapies for sickle cell disease, making one of them the first treatment in the ...