When.com Web Search

  1. Ads

    related to: duchenne muscular dystrophy clinical trials for women

Search results

  1. Results From The WOW.Com Content Network
  2. Duchenne muscular dystrophy - Wikipedia

    en.wikipedia.org/wiki/Duchenne_muscular_dystrophy

    Duchenne muscular dystrophy is the most common type of muscular dystrophy, [3] with a median life expectancy of 27–31 years. [5] [11] However, with comprehensive care, some individuals may live into their 30s or 40s. [3] Duchenne muscular dystrophy is considerably rarer in females, occurring in approximately one in 50,000,000 live female ...

  3. Vamorolone - Wikipedia

    en.wikipedia.org/wiki/Vamorolone

    In phase IIa dose-ranging clinical trial of 48 children with Duchenne muscular dystrophy (2 weeks on drug, 2 weeks off drug), vamorolone was shown to be safe and well tolerated, and showed blood biomarker data consistent with a myofiber membrane stabilization and anti-inflammatory effects, and possible loss of safety concerns. [14]

  4. Delandistrogene moxeparvovec - Wikipedia

    en.wikipedia.org/wiki/Delandistrogene_moxeparvovec

    Delandistrogene moxeparvovec, sold under the brand name Elevidys, is a recombinant gene therapy used for the treatment of Duchenne muscular dystrophy. [3] It is designed to deliver into the body a gene that leads to production of Elevidys micro-dystrophin that contains selected domains of the dystrophin protein present in normal muscle cells. [3]

  5. Sarepta's new Duchenne drug outperforms bestseller ... - AOL

    www.aol.com/news/sarepta-says-experimental...

    (Reuters) -Sarepta Therapeutics said on Monday its new experimental drug for Duchenne muscular dystrophy (DMD) was far more effective in increasing levels of a key protein than its bestselling ...

  6. Golodirsen - Wikipedia

    en.wikipedia.org/wiki/Golodirsen

    Golodirsen is one of the very few FDA-approved exon-skipping therapy for Duchenne muscular dystrophy, although the clinical benefits of the medication are yet to established. [1] [3] While the development of golodirsen needed huge financing, it is only applicable to a small subset of people with Duchenne muscular dystrophy.

  7. Pfizer reports patient death in Duchenne gene therapy study - AOL

    www.aol.com/news/pfizer-reports-patient-death...

    The trial is testing boys 2 to three years of age with DMD, a genetic muscle wa ... tested in a mid-stage trial for a muscle-wasting disorder called Duchenne muscular dystrophy(DMD), the drugmaker ...

  1. Ads

    related to: duchenne muscular dystrophy clinical trials for women